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Gene Therapy Research Intern

Sarepta Therapeutics is seeking a motivated individual to provide laboratory support, perform experiments, collect and analyze data on in vitro and in vivo studies to investigate gene therapies for rare genetic diseases. Activities will include assessment of protein expression, and/or RNA expression in models of neuromuscular disorders.


This project will examine protein-based biomarkers our in limb-girdle muscular dystrophy (LGMD) models. In vivo and in vitro models will be leveraged to assess treatment responses to our therapies. This important work will help establish markers that can be used to asses efficacy of our treatment in the clinic.


Primary Responsibilities Include:

  • Assists in conducting experiments at the direction of scientists, performs general tasks and routine laboratory functions using a variety of assay formats such as, protein isolation, Western blot, and SimpleWestern.
  • Performs general laboratory maintenance and helps to maintain a clean and safe working environment while ensuring compliance with GCP/GLP guidelines.
  • Troubleshoots routine technical challenges and contributes to their resolution.
  • Maintains compliant laboratory records, consistently and accurately documents all laboratory activities in laboratory notebooks and internal technical reports
  • Performs other related duties as assigned.


Desired Education and Skills: 

  • 1 semester of relevant experience in a laboratory setting is a plus
  • Knowledge of Western blot, qPCR, and other molecular assays.
  • Knowledge of limb-girdle muscular dystrophies and muscle biology is a plus
  • Ability to execute sample handling and analysis with strict adherence to laboratory methods.
  • Proficiency with computer productivity software (i.e. Word, Excel, etc).
  • Strong math-based reasoning, problem solving and data analysis skills.
  • Excellent written and verbal communication skills.
  • Desire to work in a dynamic, fast-paced team environment and to make a difference in the lives of people through our innovative medicines

Program Timeline: 

This application is for a 10 or 12-week summer internship program that will either start on May 28th or June 10th.  

The program will conclude on August 16th, 2024.  


This is a facility-dependent position where in-office presence is required four-five days a week. 


This position requires work on site at one of Sarepta’s facilities in the United States.


The targeted salary range for this position is $21 - $25 per hour depending upon years of education completed and nature of role.


Candidates must be authorized to work in the U.S.

Sarepta Therapeutics offers a competitive compensation and benefit package.

Sarepta Therapeutics is an Equal Opportunity/Affirmative Action employer and participates in e-Verify.